{"product_id":"rna-therapeutics-institute-rna-therapeutics-from-concept-to-clinic-2025","title":"RNA Therapeutics Institute RNA Therapeutics From Concept to Clinic 2025","description":"\u003cul\u003e\n  \u003cli\u003eTarget Audience: R\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategy professionals, manufacturing\/operations managers\u003c\/li\u003e\n  \u003cli\u003eSample video: contact me for sample video\u003c\/li\u003e\n  \u003cli\u003eInformation:\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp\u003eA translational, bench-to-bedside program covering the full lifecycle of RNA medicines. Faculty connect platform science (siRNA, ASO, mRNA, saRNA, emerging circular RNA) with delivery, CMC, regulatory strategy, and clinical development—so teams can move candidates efficiently and safely toward approval.\u003c\/p\u003e\n\u003cp\u003eWhat You Will Learn\u003c\/p\u003e\n\u003cp\u003eModality selection \u0026amp; design: choosing siRNA vs. ASO vs. (sa)mRNA vs. circRNA; chemistries, modifications, stability\u003c\/p\u003e\n\u003cp\u003eDelivery systems: LNPs, GALNAc conjugates, polymer\/peptide carriers, local vs. systemic administration\u003c\/p\u003e\n\u003cp\u003ePreclinical translation: in vitro\/in vivo models, PK\/PD, biodistribution, immunogenicity, off-target assessment\u003c\/p\u003e\n\u003cp\u003eCMC fundamentals: process development, analytics, release\/stability testing, scale-up, and tech transfer\u003c\/p\u003e\n\u003cp\u003eClinical development: FIH design, dose selection, biomarkers, patient selection, endpoints, safety monitoring\u003c\/p\u003e\n\u003cp\u003eRegulatory \u0026amp; quality: IND\/IMPD strategy, comparability, potency assays, pharm-tox expectations, risk management\u003c\/p\u003e\n\u003cp\u003eManufacturing operations: raw materials, supply chain, single-use workflows, contamination control, cost drivers\u003c\/p\u003e\n\u003cp\u003eData \u0026amp; tools: sequence optimization, secondary structure prediction, bioinformatics\/AI for target\/off-target profiling\u003c\/p\u003e\n\u003cp\u003eEvent Details\u003c\/p\u003e\n\u003cp\u003eFormat: Case-based lectures, panel Q\u0026amp;A, and short technical workshops\u003c\/p\u003e\n\u003cp\u003eStructure: Concept\/design → delivery\/PKPD → CMC\/manufacturing → clinical\/regulatory → commercialization\u003c\/p\u003e\n\u003cp\u003eTakeaways: Checklists, study-design templates, and CMC\/quality worksheets for immediate use\u003c\/p\u003e\n\u003cp\u003eWho Should Attend\u003c\/p\u003e\n\u003cp\u003eR\u0026amp;D scientists, CMC\/quality leaders, translational and clinical teams, regulatory\/strategic affairs, manufacturing\/operations managers, platform founders, investors, and trainees entering the RNA space.\u003c\/p\u003e\n\u003cp\u003eWhy Attend\u003c\/p\u003e\n\u003cp\u003eReplace trial-and-error with validated design and development playbooks\u003c\/p\u003e\n\u003cp\u003eAnticipate regulatory and manufacturing pitfalls early to de-risk timelines\u003c\/p\u003e\n\u003cp\u003eAlign discovery, CMC, and clinical groups around practical, decision-ready tools\u003c\/p\u003e\n\u003cul\u003e\n  \u003cli\u003eTopics:\u003c\/li\u003e\n\u003c\/ul\u003e\n\u003cp\u003e*Note: these are continuous video recordings during the conference, they include individual lectures mentioned in the Detail section below\u003c\/p\u003e\n\u003cp\u003eJune 25, 2025.mp4\u003c\/p\u003e\n\u003cp\u003eJune 26, 2025.mp4\u003c\/p\u003e\n\u003cp\u003eJune 27, 2025.mp4\u003c\/p\u003e\n\u003cp\u003e* Detail: Schedule\u003c\/p\u003e","brand":"Medicalcoursespro","offers":[{"title":"Default Title","offer_id":46405798002884,"sku":null,"price":52.0,"currency_code":"USD","in_stock":true}],"url":"https:\/\/medicalcoursespro.com\/products\/rna-therapeutics-institute-rna-therapeutics-from-concept-to-clinic-2025","provider":"Medicalcoursespro","version":"1.0","type":"link"}